Adrenoleukodystrophy Treatment News and Symptoms Information

What is Adrenoleukodystrophy?

(Symptoms, Causes & Treatment)

According to the U.S. National Library of Medicine, adrenoleukodystrophy refers to several closely related disorders that disrupt the breakdown of certain fats. These disorders are passed down from parent to child as an X-linked genetic trait. It affects mostly males, although some women who are carriers can have milder forms of the disease. It affects about 1 in 20,000 people from all races.

There are 3 major categories of disease:

  • Childhood cerebral form — appears in mid-childhood (at ages 4 to 8)
  • Adrenomyelopathy — occurs in men in their 20s or later in life
  • Impaired adrenal gland function (called Addison disease or Addison-like phenotype) — adrenal gland does not produce enough steroid hormones

See below for updated news and information regarding Adrenoleukodystrophy including new medical research, treatment options and advancements. 

Latest Adrenoleukodystrophy Treatment News and Research

Sunshine from Spain: Minoryx Targets Rare Genetic Diseases (blog)Jan 20, 2017
Mission: Minoryx Therapeutics is focused on a group of rare genetic diseases like X-Linked Adrenoleukodystrophy (X-ALD) and other …

Stem cell-transplantation therapy for adrenoleukodystrophy: current …

Dove Medical PressJan 9, 2017
Abstract: Adrenoleukodystrophy (ALD) is a rare, X-linked peroxisomal disorder of impaired very long-chain fatty-acid metabolism. It results from …

Viking’s in-vivo model of X-Linked Adrenoleukodystrophy study a

Drug Target ReviewSep 27, 2016
Viking Therapeutics announced the presentation of positive data from a proof-of-concept study of VK0214 in a mouse model of X-linked …

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