Beta Thalassemia Treatment News and Information

What is Beta Thalassemia? (Definition)

Beta thalassemias (β thalassemias) represent a relatively rare group of inherited blood disorders. They are forms of thalassemia caused by reduced or absent synthesis of the beta chains of hemoglobin that result in variable outcomes ranging from severe anemia to clinically asymptomatic individuals. Beta thalassemias are caused by mutations in the HBB gene on chromosome 11, inherited in an autosomal recessive fashion. The severity of the disease depends on the nature of the mutation.

See below for updated news and information regarding Beta Thalassemia including new research, treatments and advancements. 

Latest Beta Thalassemia News

New Gene Editing Technology May Offer Future Hope for Blood Disorders Like Beta Thalassemia and Sickle Cell

(Carnegie Mellon University / EurekAlert) According to a recent press release, a new gene-editing system developed by Carnegie Mellon University and Yale University research scientists has cured a genetic blood disorder in living mice using a simple IV treatment. Unlike the popular CRISPR gene-editing technique, the new technology can be administered to living animals and it significantly decreases unwanted, off-target ...
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